Exon-Skipping to Gene Therapy: What's Next for Duchenne...

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2025-02-28 05:34:35 -

Exon-Skipping to Gene Therapy: What's Next for Duchenne Muscular Dystrophy?

Duchenne muscular dystrophy (DMD) is a rare, progressive neuromuscular disorder caused by mutations in the dystrophin gene. While exon-skipping therapies have played a key role in advancing the Duchenne muscular dystrophy treatment landscape, researchers are now exploring alternative therapeutic strategies to enhance patient outcomes. Existing Treatment Options for Duchenne Muscular...

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